Designation recognizes the commitment to improving access and care for patients with rare diseases November 04, 2021 The Rare Disease Institute (RDI) at Children’s National Hospital announced its designation as a NORD Rare Disease Center of Excellence, joining a highly select group of […]
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Scientists find that three rare cannabinoids reduce seizures in mice — ScienceDaily
Investigate from pharmacologists at the University of Sydney offers new insights into how cannabis extracts may function to address epilepsy. The examine for the 1st time stories that 3 acidic cannabinoids discovered in cannabis lowered seizures in a mouse model of Dravet syndrome, an intractable variety of childhood epilepsy. The […]
The Children’s National Hospital Rare Disease Institute and Takeda Partner to Standardize Care for Patients with Rare Diseases
A 5-yr motivation from Takeda will aid Children’s Nationwide launch a to start with-of-its-form scarce disease clinical protocol method. March ten, 2021 Children’s Nationwide Healthcare facility and Takeda Pharmaceutical Firm Constrained (TSE:4502/NYSE:TAK) (“Takeda”) today introduced the generation of the Uncommon Condition Medical Exercise Protocols (Uncommon-CAP) method, which will create a […]
Reducing urinary protein for patients with rare kidney disease slows kidney decline
Even devoid of comprehensive remission, reducing proteinuria in people with FSGS will allow their kidneys to operate for a longer period and extends time to stop stage kidney condition August twelve, 2020 Lessening the quantity of protein in the urine of people with focal segmental glomerulosclerosis (FSGS), a uncommon condition […]